[注] MPS1 (mucopolysaccharidosis I)[出典] "Brain and visceral gene editing of mucopolysaccharidosis I mice by nasal delivery of the CRISPR/Cas9 system" Vera LNP [..] Baldo G, Teixeira HF. J Gene Med. 2022-01-14. https://doi.org/10.1002/jgm.3410　ムコ多糖 …

1．CRISPR/Cas9ツールによる麹菌におけるコウジ酸合成遺伝子kojA, kojR, kojTの一重，二重，三重変異体の構築[出典] "Construction of single, double, or triple mutants within kojic acid synthesis genes kojA , kojR , and kojT by the CRISPR/Cas9 tool in Aspergill …

[注] DUB (Deubiquitinase); USP11 (Ubiquitin carboxyl-terminal hydrolase 11)[出典] "Genome-Wide CRISPR/Cas9-Based Screening for Deubiquitinase Subfamily Identifies Ubiquitin-Specific Protease 11 as a Novel Regulator of Osteogenic Differentiation" Kaushal K …