[出典] "RNA-Targeting CRISPR/CasRx system relieves disease symptoms in Huntington’s disease models" Lin Y, Li C, Chen Y [..] Yan S. Mol Neurodegener. 2025-01-13. https://doi.org/10.1186/s13024-024-00794-w 　ハンチントン病（HD）は、HTT 遺伝子におけるCAG …

[出典] "A high-fidelity CRISPR-Cas13 system improves abnormalities associated with C9ORF72-linked ALS/FTD" McCallister TX [..] Gaj T. Nat Commun. 2025-01-08. https://doi.org/10.1038/s41467-024-55548-5 [所属] U Illinois Urbana-Champaign (The Grainger Colle …

2025-01-11 Nature Communications 誌刊行論文の書誌情報を追記2024-02-10 bioRxiv 投稿に準拠した初稿[出典] "Dual-targeting CRISPR-CasRx reduces C9orf72 ALS/FTD sense and antisense repeat RNAs in vitro and in vivo" Kempthorne L, Vaizoglu D, Cammack AJ [..] Is …