crisp_bio

RIKEN (NISLO, WDCM ...) - NIG (DDBJ/CIB, WDCM, OECD BRC, GBIF, JST BIRD, TPRP ...) - FREE

タグ:遺伝子診断・治療

[出典] REVIEW "Advances in CRISPR/Cas9 Genome Editing for the Treatment of Muscular Dystrophies" Fatehi S, Marks RM, Rok MJ, Perillat L, Ivakine EA, Cohn R. Hum Gene Ther 2023-04-29. https://doi.org/10.1089/hum.2023.059 [著者所属] U Toronto. デュシェンヌ ... もっと読む
このエントリーをはてなブックマークに追加

[出典] "Tau-targeting antisense oligonucleotide MAPTRx in mild Alzheimer's disease: a phase 1b, randomized, placebo-controlled trial" Mummery CJ, Börjesson-Hanson A, Blackburn DJ et al. Nat Med. 2023-04-24. https://doi.org/10.1038/s41591-023-02326-3 [著 ... もっと読む
このエントリーをはてなブックマークに追加

[出典] "Editing the core region in HPFH deletions alters fetal and adult globin expression for treatment of β-hemoglobinopathies" Venkatesan V [..] Thangavel S. Mol Ther Nucleic Acids. 2023-04-26. https://doi.org/10.1016/j.omtn.2023.04.024 [著者所属] Cen ... もっと読む
このエントリーをはてなブックマークに追加

[出典 "A Conditional Pol II mono-promoter drives HIV-inducible CRISPR mediated Cyclin T1 suppression and HIV inhibition" Chinnapaiyan S [..] Unwalla HJ. Mol Ther Nucleic Acids. 2023-04-13 (Accepted) https://doi.org/10.1016/j.omtn.2023.04.011 [著者所属] Fl ... もっと読む
このエントリーをはてなブックマークに追加

[出典] "CRISPR-Cas9 mediated endogenous utrophin upregulation improves Duchenne Muscular Dystrophy" Guiraud S [..] Amendola M. bioRxiv. 2023-04-19 [preprint] https://doi.org/10.1101/2023.04.18.536394  [著者所属] Genethon, U Paris-Sacla, U Evry, Museum Na ... もっと読む
このエントリーをはてなブックマークに追加

↑このページのトップヘ